Novartis reports Phase III efficacy and safety outcomes of SMA treatment
The development programme for the therapy has encompassed over 170 SMA subjects.
Cytiva Pipe dream to pipeline WP 3
Amgen and Kyowa Kirin’s rocatinlimab trial for atopic dermatitis meets endpoints
Elixirgen’s gene therapy shows promise in telomere biology disorders
Success for YolTech’s hyperoxaluria in vivo gene therapy in early-stage trial
Sensorion’s Phase I/II gene therapy trial to continue with DMC recommendation
Struggling bluebird bio to go private for less than $30m
Boehringer and partners commence gene therapy trial for cystic fibrosis
Solid Biosciences’ stock soars on early success in DMD gene therapy trial
