Delivering gene therapy directly to the brain for AADC deficiency
PTC Therapeutics’ gene therapy delivered directly to the brain is yielding life-changing results in children with AADC deficiency.
By
Genomics
Latest in
Genomics
FDA approves first trial investigating CRISPR gene editing as HIV cure
A new paradigm for HIV treatment is on the horizon as FDA gives nod for startup to begin trials of…
By
Leading regenerative medicine advocacy group leverages GlobalData’s datasets to highlight a record year
The Alliance for Regenerative Medicine’s report reveals the data behind a “year of firsts and records” for the sector.
By
uniQure gene therapy found “highly unlikely” to be cause of liver cancer case
Netherlands-based gene therapy developer uniQure has announced the results of a comprehensive investigation into the case of hepatocellular carcinoma (HCC)…
By
AD/PD 2021: A New Neuro-Regenerative Therapeutic Approach Targeting Protein Kinase C for the Treatment of Alzheimer’s Disease
At the 15th International Virtual Conference on Alzheimer’s disease (AD) and Parkinson’s disease (PD) 2021, a clinical-stage biotech company based…
By
Partner content
GSK to expand clinical trial manufacturing capacity at CGT Catapult site in UK
GlaxoSmithKline (GSK) will expand its presence at the UK Cell and Gene Therapy (CGT) Catapult’s Stevenage facility to carry out…
MANTA and MANTA-RAy Safety Readouts Boost Jyseleca’s Prospects in the US
On March 4, Galapagos announced pooled interim results from its ongoing MANTA and MANTA-RAy testicular safety studies for Jyseleca (filgotinib)…
UK Covid-19 Vaccine Administration at 300 shots per 1,000 population, while vaccine rates low elsewhere in europe
With new SARS-CoV-2 variant strains appearing, the global race to control the COVID-19 pandemic through immunization is on. Europe remains…